Clinical research
With the vision to be a premier muscular dystrophy center, researchers and providers at CIMR are leading the way in treating inherited muscle disorders. Clinicians work directly with patients to participate in ongoing clinical trials and implement the latest advancements in treatments.
VCU is also a site for international research networks focusing on limb-girdle muscular dystrophy (LGMD) and myotonic dystrophy (MD), with Nicholas Johnson, M.D., director of CIMR, serving as coordinating principal investigator:
- Genetic Resolution and Assessments Solving Phenotypes in LGMD (GRASP-LGMD) Consortium
- Myotonic Dystrophy Clinical Research Network
Current and Upcoming Natural History Trials
- Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- Assessing Pediatric Endpoints in DM1 (ASPIRE-DM1)
- Defining Endpoints in Becker Muscular Dystrophy
- Trial Readiness and Endpoint Assessment in LGMD R1
- Coming soon: Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension (TREAT-EXT)